PTC, Genzyme muscular dystrophy drug falls short

Wed, 03/03/2010 - 6:17am
The Associated Press

PTC Therapeutics Inc. and Genzyme Corp. said Wednesday their potential muscular dystrophy treatment did not meet its primary goal in a midstage study.

In the study, ataluren failed to meet its goal of improving walking distance. Muscular dystrophy is a genetic condition that weakens the muscles and hampers walking ability. Results did show that the drug was well tolerated, the companies said.

The results of the 48-week study are preliminary, the companies said.

Ataluren is also being studied as a potential treatment for a form of cystic fibrosis and hemophilia.

Shares of Genzyme, based in Cambridge, Mass., rose 36 cents to $57.18 in morning trading. PTC is based in South Plainfield, N.J.


Share this Story

You may login with either your assigned username or your e-mail address.
The password field is case sensitive.